Research
During the 2020 Ipnet General Assembly on December 4th, 2020, 5 presentations came out from the Scientific Meeting. There are videos available following the links below.
Scientific Meeting Ipnet Association
December 4 th , 2020 at 15:30 – 18:30 CET
1. Givosiran: Efficacy, safety and therapeutic scheme, by Eliane Sardh, Stockholm:
2020 status of Givosiran, by Eliane Sardh
2. Iron deficiency as a treatment of CEP, by Emmanuel Richard, Bordeaux:
Iron deficiency: a treatment of CEP, by Emmanuel Richard
3. Generation and Characterization of an Inducible Hepatocyte-specific ALAS1 Knockout Mouse
Model, by Makiko Yasuda, New York
4. Farewell Biorad: MS methods for PBG/ALA, by Thibaud Lefebvre, Paris
2020 MS methods for PBG/ALA, by Thibaud Lefebvre
5. Highlights from the MT-7117 Dersimelagon Phase 2 Muticenter, Double-Blind, Placebo-
Controlled Trial in 102 EPP Patients, by Robert Desnick, New York
