Report 2020 General Assembly
General Assembly Meeting Ipnet Association
December 4 th , 2020 at 12:00 – 14:00 CET
- Opening and Welcome, by Sverre Sandberg
- Approval of Minutes GA Meeting Sep 9 th , 2019, by Eliane Sardh
- Presentation of EB Board 2021-22, by Sverre Sandberg
- Report of Ipnet activities, by Sverre Sandberg
- Financial information, by Janneke Langendonk
- Reports from Working Group Chairs:
Laboratory WG:
2020 Report by Aasne Aarsand, Laboratory Working Group Chair
Acute Hepatic Porphyria WG:
2020 Report by Penelope Stein, Acute Hepatic Porphyria Clinical Working Group Chair
Cutaneous Porphyria WG:
2020 Report by Michael Badminton, Cutaneous Porphyria Working Group Chair
Research & Development WG:
2020 Report by Laurent Gouya, Research and Development Working Group Chair
Website WG:
2020 Report by Caroline Schmitt, Website Working Group Chair
- Conclusion and Closure, by Sverre Sandberg
Scientific Meeting Ipnet Association
December 4 th , 2020 at 15:30 – 18:30 CET
1. Givosiran: Efficacy, safety and therapeutic scheme, by Eliane Sardh, Stockholm:
2020 status of Givosiran, by Eliane Sardh
2. Iron deficiency as a treatment of CEP, by Emmanuel Richard, Bordeaux:
Iron deficiency: a treatment of CEP, by Emmanuel Richard
3. Generation and Characterization of an Inducible Hepatocyte-specific ALAS1 Knockout Mouse
Model, by Makiko Yasuda, New York
4. Farewell Biorad: MS methods for PBG/ALA, by Thibaud Lefebvre, Paris
2020 MS methods for PBG/ALA, by Thibaud Lefebvre
5. Highlights from the MT-7117 Dersimelagon Phase 2 Muticenter, Double-Blind, Placebo-
Controlled Trial in 102 EPP Patients, by Robert Desnick, New York